Journal Article

Structural characterization of antibody-responses following Zolgensma treatment for AAV capsid engineering to expand patient cohorts

Author(s)

Mario Mietzsch/McKnight Brain Institute; College of Medicine
Jane Hsi/McKnight Brain Institute; College of Medicine
Austin R. Nelson/McKnight Brain Institute; College of Medicine
Neeta Khandekar/The University of Sydney and Sydney Children's Hospitals Network
Ann-Maree Huang/The University of Sydney and Sydney Children's Hospitals Network
Nicholas J.C. Smith/Women's and Children's Hospital, Women's and Children's Health Network
Jon Zachary/McKnight Brain Institute; College of Medicine
Lindsay Potts/McKnight Brain Institute; College of Medicine
Michelle A. Farrar/UNSW Medicine; Sydney Children's Hospital
Paul Chipman/Interdisciplinary Center of Biotechnology Research, University of Florida
Mohammad Ghanem/Helsinki Institute of Life Science, University of Helsinki
Ian E. Alexander/The University of Sydney; Sydney Children's Hospitals Network
Grant J. Logan/The University of Sydney; Sydney Children's Hospitals Network
Juha T. Huiskonen/Helsinki Institute of Life Science, University of Helsinki
Robert McKenna/McKnight Brain Institute; College of Medicine University of Florida

Nature Communications

April 19, 2025